Elevating Safety & Efficiency of Gene Therapy Programs with Direct Intra-CSF Administration Routes

Time: 11:30 am
day: Conference Day Two


  • Tailoring capsids for specific intra-CSF delivery routes depending on the indication to be targeted
  • Identifying the optimal dosage window for therapeutics delivered by ICM to achieve desired expression levels in the target of interest
  • Mitigating risks of brainstem injury during ICM delivery