Elevating Safety & Efficiency of Gene Therapy Programs with Direct Intra-CSF Administration Routes
Time: 11:30 am
day: Conference Day Two
Details:
- Tailoring capsids for specific intra-CSF delivery routes depending on the indication to be targeted
- Identifying the optimal dosage window for therapeutics delivered by ICM to achieve desired expression levels in the target of interest
- Mitigating risks of brainstem injury during ICM delivery
