Optimizing Technical Workflow to Safely & Effectively Deliver Gene Therapies via ICM Administration
Time: 11:00 am
day: Day One - Morning - Track B
Details:
- Leveraging intra-cisterna magna (ICM) delivery to maximize vector distribution throughout the CNS
- Key technical and clinical considerations for precise and reproducible administration to the cisterna magna
- Evaluating neuroimaging strategies to guide and confirm targeted delivery
- Exploring scalability, safety, and dose optimization for broader clinical application in genetic CNS disorders